071 – John Crowley Saved His Kids’ Lives By Finding a Cure to Pompe Disease

Meet John Crowley, a special father of three kids with special needs. Two of those children have a rare genetic disorder called Pompe disease. John and his wife Aileen were told that Meghan and Patrick would not live very long. So, they took matters into their own hands and helped develop a drug that successfully treats the disorder. They formed a successful RX company, Amicus, whose mission is to find treatments for rare diseases. Their story was told in a book, a movie starring Harrison Ford and by the President of the United States in a joint session of congress. And

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